Gene therapy, a technique that is revolutionizing the treatment of multiple genetic conditions, including eye and muscle diseases and blood disorders, requires efficient and specific delivery of the ...

Gene therapy, a technique that is revolutionizing the treatment of multiple genetic conditions, including eye and muscle diseases and blood disorders, requires efficient and specific delivery of the ...

Two common and potentially deadly heart diseases can be caused by mutations in the same gene. Surprisingly, though, these two ...

We all know to worry about fat around our waists or clogging our arteries. But now there is a new place to potentially be ...

O rgan transplants are a familiar idea. Organelle transplants, less so. Yet organelles are to cells what organs are to bodies ...

Trial achieved key objectives for safety, tolerability, pharmacokinetics and pharmacodynamicsClinical data from this trial, together with ...

WVE-N531 demonstrated statistically significant improvements in muscle biopsy measures and functional measures in patients ...

Once adapted to treat humans, the technique could potentially be used to repair heart muscle damage after a heart attack and be applied to a variety of inflammatory disorders ... percentage of these ...

“One of the cool things about natural muscle tissues is, they don’t just point in one direction. Take for instance, the circular musculature in our iris and around our trachea. And even within ...

Bone marrow is the soft, fatty tissue inside large bones like the hip and thigh bones ... Why People Get Bone Marrow Transplants Bone marrow transplants are often used to treat serious diseases and ...

This process leads to satellite cells multiplying and their daughter cells migrating to the damaged tissue. Here, they fuse with skeletal muscle and donate their nuclei to the muscle fibers ...