Gene therapy pioneer Jim Wilson and researcher Kiran Musunuru are using contrasting approaches to overcome “irrational ...
The arc of biotechnology is one of breakthroughs and struggles, writes Tim Hunt, CEO of the Alliance for Regenerative ...
In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...
A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the amount of blood the heart can pump and dramatically improves ...
Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders. Now it’s on the cusp of its first regulatory approval. Each year ...
“This is the beginning of a new era of medicine,” said Dr. Kiran Musunuru, a gene therapy researcher at the University of Pennsylvania’s Perelman School of Medicine. He added that the method ...
To date, the therapeutic results of gene therapy have been marginal. This approach holds much potential, however, especially for treating single-gene disorders, and it is therefore being actively ...
College Station gene therapy company partners with nonprofit to develop treatments for rare diseases
Together, the manufacturer and the nonprofit are developing a gene therapy treatment that could change the lives of children with conditions that currently have no cure. Childs Cure co-founders ...
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