Ipsen has suffered a setback in its marathon effort to bring palovarotene to market for ultra rare disease ... underlying FOP, which has only been diagnosed in around 900 people worldwide.

In the UK, for example, the average diagnosis of a rare disease takes around ... from ultra-rare diseases like Fibrodysplasia Ossificans Progressiva (FOP) to more prevalent, yet still rare ...

AI helped Thomas Wagner understand Alexander disease, find connection with other conditions and discover researchers who ...

Ella Rhian had never experienced any stomach problems before and lived a normal, healthy life. Then, in September 2023, the ...

Knight says that the method of transmission that Collinge identified is “extremely unusual,” and there’s no evidence that ...

Celine Dion is the best-known sufferer of this disorder, one of many autoimmune illnesses that disproportionately impact ...

A tendency to drag down those who set themselves above others, the syndrome supposedly reflects values of equality, humility ...

CINCINNATI (WXIX) - Four people including a Cincinnati police officer ... to the police SUV and it is being investigated further, FOP President Ken Kober tells FOX19 NOW. The police SUV, a 2017 ...

June 10, 2024 — Scientists have grown 'mini-guts' in the lab to help understand Crohn's disease, showing that 'switches' that modify DNA in gut cells play an important role in the disease ...

Gov. Josh Shapiro has returned to the courtroom with a new challenge to the Trump administration. On Tuesday, the governor signed on as a co-plaintiff with 22 other states and the District of ...

Early Signs of Heart Problems Linked to Smaller Brain Volumes Mar. 26, 2025 — People who have early signs ... 2025 — Many youth have heart disease risk factors by their late teens, and ...