A pair of privately-held developers of editing-based therapies have some successes to show for their recent efforts to ...

Phase 1b/2 Clinical Trial of TN-201 for Treatment of MYBPC3-Associated Hypertrophic Cardiomyopathy MyPEAK-1 Cohort 1 Data ...

On top of helping you quickly find the folders or files you're looking for, the PowerToys Run feature can also perform several other functions, from converting units to executing system commands. And ...

Alternative splicing (AS) of pre-mRNA plays a crucial role in tissue-specific gene regulation, with disease implications due to splicing defects. Predicting and manipulating AS can therefore uncover ...

Q4 2024 Earnings Call Transcript March 5, 2025 Ocugen, Inc. reports earnings inline with expectations. Reported EPS is $-0.05 EPS, expectations were $-0.05. Operator: Good morning, and welcome to ...

Novartis announces positive data from phase III study of intrathecal onasemnogene abeparvovec in broad patient population with SMA: Basel Friday, March 21, 2025, 11:00 Hrs [IST] N ...

Reported positive initial data from INSPIRE DUCHENNE trial of next-generation Duchenne gene therapy candidate, SGT-003; In mid-2025, ...

We look forward to building upon the encouraging data generated to date and engaging with health authorities to explore the registrational pathway for this promising, one-time therapy to address a ...

Adverum's inclusion in ARTEMIS of both treatment-naive and treatment-experienced patients is intended to address a broad patient population ... Ixo-vec utilizes a proprietary vector capsid, AAV.7m8, ...

ITV Studios has added another French scripted label to its ranks. L/Intruse will sit within Tetra Media Studio, the French production subsidiary of UK network ITV’s production and sales arm.

Although Jack has gracefully accepted his ‘nepo baby’ label, he’s said that he has “tried to work as hard as I possibly can to prove that I deserve to walk through that door.” ...

March 13, 2025 – VAST Data, the AI data platform company, today announced new enhancements to the industry-leading VAST Data Platform, making it the first and only system in the market to unify ...