A pair of privately-held developers of editing-based therapies have some successes to show for their recent efforts to ...

Alternative splicing (AS) of pre-mRNA plays a crucial role in tissue-specific gene regulation, with disease implications due to splicing defects. Predicting and manipulating AS can therefore uncover ...

Sarepta Therapeutics said early Tuesday that a patient had died after receiving its gene therapy Elevidys, which treats the rare genetic condition Duchenne muscular dystrophy. A young man with ...

Novartis announces positive data from phase III study of intrathecal onasemnogene abeparvovec in broad patient population with SMA: Basel Friday, March 21, 2025, 11:00 Hrs [IST] N ...

Operator Good afternoon, ladies and gentlemen, and welcome to the INOVIO Pharmaceuticals fourth quarter 2024 financial results conference call. At this time, all lines are in listen-only mode.

Alvvays fans have been waiting a long time for their limited edition vinyl, but it sounds like the wait will be over soon.

Although Jack has gracefully accepted his ‘nepo baby’ label, he’s said that he has “tried to work as hard as I possibly can to prove that I deserve to walk through that door.” ...

EXCLUSIVE: Phoenix-based multicultural film and animation outfit Sandoval Studios is working on an adaptation of The Case For Miracles in collaboration with author Lee Strobel and Harper Collins ...

INmune Bio's high-upside potential with CORDStrom for RDEB and XPro for Alzheimer's, offering up to 144.8x returns. Click ...

New Delhi, Delhi, India <li /> Sickle cell advance research centre to be set up by Sanmat <li /> Sanmat to support the state ...

The 'Quad Workshop on Pandemic Preparedness for the Indo-Pacific Region' commenced on Monday and will go on till March 19 ...

Microglia are brain-resident macrophages playing pivotal roles in CNS development and homeostasis. Yet, the cellular and molecular basis governing microglia maintenance ...